Translating Next-Generation Science Into Transformative Gene TherapiesLearn About Our Programs

Programs Encoded is building an internally developed pipeline of best- and potentially first-in-class therapies focused on neurological disorders.

Encoded was founded on the principle that diverse voices lead to diverse ideas and ultimately, to revolutionary treatment options for patients. Our diversity – whether gender, ethnicity, sexual …

Ever wondered what it takes to make a gene therapy? Join us on a virtual lab tour at Encoded’s headquarters in South San Francisco. Meet a few of our talented scientists ready to explain what …

“The support we have received from this visionary group of investors will allow us to develop into a fully-integrated therapeutics company and establish Encoded as a leading innovator in gene therapy.”

Encoded will be providing additional updates on its research pipeline, which is focused on both rare genetic and common disease programs, in addition to clinical progress with ETX101 for Dravet …

Encoded Therapeutics to Present Interim Phase 1/2 Clinical Data on ETX101, the First One-time Gene Therapy in Development for Dravet Syndrome, at the 2025 American Epilepsy Society Annual Meeting

Dec 16, 2025 · Encoded Therapeutics is a clinical-stage genetic medicines company developing one-time therapies for severe neurological disorders. Our vector engineering platform enables highly …

Encoded carefully designs clinical studies to assess safety and efficacy of its investigational gene therapies for the treatment of neurological disorders. People considering enrolling their child in an …

Each one of our programs is born at Encoded as a solution to a biological problem. We combine genomics-driven data with internal biological expertise and access to worldwide thought leaders to …